Guangping Gao, PhD
Research Focus - Adeno-associated Virus: Biology, Vectorology, and Applications for In Vivo Gene Therapy
- The molecular genetics and pathomechanism of inborn errors of metabolism in the central nervous system
- Natural evolution, host interactions, and genetic fate of adeno-associated virus (AAV)
- Vectorology, transduction biology, and structural biology of AAV
- Novel enabling technology platform development for AAV vectors, genome editing, animal modeling, and RNA therapeutics
- Interventional in vivo gene therapy for gene replacement, silencing, addition, and editing
Representative Publication
Wang D, Tai PWL, Gao G. Adeno-associated virus vector as a platform for gene therapy delivery. Nat Rev Drug Discov. 2019;18(5):358-378.